The nerve cell-targeting EXG001-307 seems to have a better safety profile than Zolgensma, showing fewer adverse effects on ...

Impressed by the accurate portrayal of emergency rooms on "The Pitt," columnist Sherry Toh hopes to see her own rare disease ...

Columnist Helen Baldwin observes SMA Awareness Month by recalling her son's short life with the disease, as well as all she ...

Columnist Connie Chandler explains how letting go of her "ideal" checklist helped her build a diverse and reliable team of ...

A man with SMA and no history of diabetes developed diabetic ketoacidosis, showing how muscle loss may disrupt metabolism.

SMA Awareness Month is a time to shine a light on the everyday challenges and celebrations with this disease, writes ...

In an exclusive Q&A, a Biogen exec discussed the developer's quest to 'rapidly' bring its experimental SMA therapy salanersen ...

Columnist Ari Anderson still needs to expand his team of home-care nurses, but the ones he has always go the extra mile.

Zolgensma is approved for any type of SMA related to SMN1 mutations, but shouldn't be administered to anyone with an active ...

Candis Welch shares her experience with SMA and addresses common misconceptions about disability with clarity, humor, and honesty.

Columnist Connie Chandler says that people in a wheelchair like to dance like everyone else and deserve some technical ...

For Cure SMA, August is the time to shine a spotlight on the SMA community and to help raise awareness about the rare genetic ...