Alexa Beichler says switching her boys' medical grade formula to another brand is nearly impossible as the transition can take weeks Anya Leon is a Senior News Editor and the Parents Editor for PEOPLE ...

Alexa Beichler, whose sons were born with classic phenylketonuria (PKU) and need medical-grade formula, finally got a new shipment after stretching what they had left amid the shortage Georgia Slater ...

Contributors from the PKU community discuss the implications of redefining ‘unmet medical need’ in the EU’s pharmaceutical ...

“Lifting the Limits for PKU” raised $350,000 at an event held Sept. 5 at the Secret Garden in Rancho Santa Fe. The event raises funds to support NPKUA (National PKU Alliance) whose mission “is to ...

Researchers at The University of Texas MD Anderson Cancer Center have discovered a critical new factor in regulating phenylalanine metabolism and, therefore, in preventing the inherited metabolic ...

The phenylketonuria (PKU) test is a diagnostic tool used to test infants for phenylketonuria a few days after birth. PKU is an autosomal recessive inborn error of ...

BioMarin Pharmaceutical is continuing to slim down its pipeline, this time ending work on a preclinical phenylketonuria (PKU) drug once touted as a potential successor to its approved med Palynziq.

Otsuka Pharmaceutical has picked up Boston-based Jnana Therapeutics for $800 million so the Japanese biotech can get its hands on a clinical-stage oral phenylketonuria (PKU) drug. Under the terms of ...

Otsuka Pharmaceutical is broadening its scope in rare disease, striking a deal to acquire Jnana Therapeutics and its lead drug candidate, a small molecule on track for pivotal testing in a metabolic ...

Peking University, April 09, 2025: Groundbreaking cancer immune variant screenings and a new controlled polymerization method could reshape how we approach treatment and material synthesis. Here are ...